development pipeline

Pipeline – Drugs for rare diseases

NAME	ORIGINATOR	INDICATION	DEVELOPMENT STATUS
Carbaglu®	Orphan Europe (Recordati)	NAGS deficiency	Pre-registration in US
Carbaglu®	Orphan Europe (Recordati)	Organic acidemias	Filed in EU Phase III in U.S.A.
Cystadrops®	Orphan Europe (Recordati)	Ocular cystinosis	Phase II
Normosang®	Orphan Europe (Recordati)	Hepatic porphyria	Pre-registration in US